Gene Therapy for Dogs With Inherited Blinding Eye Disease Set for Human Trials
Summary: A groundbreaking gene therapy proven successful in treating an inherited, blinding eye disease in dogs is now poised for clinical trials in humans with the rare condition retinitis pigmentosa.
The therapy, which halts vision loss by introducing a normal copy of the CNGB1 gene, could potentially benefit around 2 million people affected worldwide.
Key Facts:
The gene therapy has been successfully trialed in dogs with an inherited eye disease and is now ready for clinical use in human patients suffering from retinitis pigmentosa.
Retinitis pigmentosa affects approximately 2 million people worldwide, with 100,000 cases in the US alone.
The therapy works by introducing a normal copy of the CNGB1 gene, rescuing normal function in rod cells, preserving cone function, and preserving retinal structure by stopping photoreceptor degeneration.
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https://neurosciencenews.com/eye-disease-gene-therapy-23122/
= new reply since forum marked as read
in eradicating diseases. The cost is another story, I’m told.
